MRC Path - Mutation Detection Methods

OLIGO LIGATION ASSAY

Basis of the test:

Two oligonucleotide probes are hybridised to adjacent sequences of PCR amplified target DNA with the join situated at the position of a known mutation site. DNA ligase covalently joins the two oligonucleotide probes only if they are perfectly hybridised which will only occur if no mutation is present. Initial studies tagged one probe with biotin and the other with a reporter molecule such as digoxygenin. On transfer to streptavidin coated microtitre plates washing will remove the reporter labelled probe unless ligation has occurred. Signal detection will therefore only occur if the mutation is not present (or visa versa depending on the design of the probe). This technology was improved when Tobe et al developed a method of typing two alleles in a single microtitre well by marking each of the allele specific primers with different enzyme reporter molecules so that two different colours can be produced.
The fact that this technique does not involve centrifugation or electrophoresis makes it amenable to large scale automated testing.
Recent advances to the technique have replaced the biotin with mobility modifying tails and digoxygenin with fluorescent tags (FAM, HEX or TET) with the ligation products being electrophoresed and analysed on an automated sequencer. These modifications have allowed the number of known point mutation sites which can be screened at any one time to be increased and Applied Biosystems now have kits capable of screening for 31 known CF mutations in a single reaction tube and single lane of an electrophoresis run.

The Applied Biosystems CF Assay

A cocktail of fifteen pairs of primers is used to amplify regions of the CFTR gene where common mutations are located. Each amplified segment (or amplicon) is probed with three oligonucleotide probes. The common probe hybridises to the amplicon at a sequence that is present in both normal and mutant alleles and is labeled with one of three fluorescent tags.

The mutant and normal probes are allelic and can be distinguished by their length since they have varying numbers of mobility modifying tails attached. These tails were initially non-complementary Poly A or Poly C but are now composed of Pentaethylene oxide (PEO) units.

At any one locus, if the mutation is not present only the normal and common probe will form a ligation product, if a homozygous mutation is present only the mutant and common probes will ligate and in heterozygous samples both normal and mutant probes will ligate to the common probe in equal amounts but giving products of different mobility.

The rTth DNA ligase facilitates ligation by catalysing the formation of a phosphodiester bond between the 5' phosphate of the common probe and the 3' hydroxyl of either the normal or mutant probe. This reaction will ONLY occur when both probes are hybridised and perfectly matched to the complementary target amplicon.

Following ligation, the product for each amplicon has a unique combination of electrophoretic mobility and fluorescence which allows identification of the sample phenotype by size separation of the ligation product in each of the three colours (the CF kit is designed to have 10-12 blue, 10-12 green and 9-11 yellow peaks). A red labelled internal size standard allows Genescan analysis software to size products precisely, label fragment data and display fragments as labelled peaks in plot displays.

The results must then be evaluated to determine accuracy. Validation should ensure all size standard peaks are present and correct, count peaks in both the normal and negative control lanes and determine the validity of each labelled peak in the test sample lanes.

Benefits:

Useful middle step between the Zeneca CF4 or 12 mutation kits and a full rare mutation screening which is often laborious and time consuming. Results are available quickly.
Suitable to mutation detection in any gene where a number of known mutations or common polymorphisms occur - has been used for screening in a number of genes e.g. the N-acrylamine-acetyltransferase (NAT2) gene (Bigler et al) and human platelet antigen-1 (HPA-1) (Zotz et al).

Problems:

Expensive!!
Requires good quality samples (correct blood : EDTA ratio)
Many fragments fall outside the accepted peak height range and must therefore be re-examined
Some polymorphisms not detected by the kit can affect the outcome of the assay e.g. P1290P polymorphism in exon 20 causes the amplicon used to detect W1282X to completely drop out with the potential for false results. See table for other polymorphisms which may have an effect:-

Table from Applied Biosytems Cystic Fibrosis Assay Protocol

Locus of Detectable AlleleInterfering Polymorphism(s)Possibility of Diminished OLA Product for...
5071648A to G
1650C to G
I507/deltaF508 and deltaI507
5071651A to GdeltaI507/deltaF508
5081648A to G
1650C to G
deltaI507/F508 and deltaF508
5081651A to GdeltaF508
5081566T to GNo diminished OLA signal at F508 locus
Note F508C will not genotype as a separate allele, but will give the normal F508 genotype
1282
3905
4002A to GW1282, X1282, 3905 and 3905delT
621+1621+3A to G621+1G and 621+1T
11623617G to TR1162 and X1162

When a compound heterozygote occurs within the hotspot region of exon 11 the corresponding normal allele for each mutation may not be detected and consequently mutations of this region must be re-examined.
Other problems with interpretation include dye bleed through because of an incorrect matrix and raised base lines which can interfere with peaks
Time required on the automated sequencer may make the test unsuitable for routine use for all CF samples

References:

Bigler J, Chen C and Potter JD. Determination of human NAT2 acetylator genotype by oligonucleotide ligation assay. Biotechniques. 1997, 22 (4):682-4
Tobe VO, Taylor SL, Nickerson DA. Single-well genotyping of diallelic sequence variations by a two- color ELISA-based oligoligation assay. Nuc Acid Res. 1996, 24 (19): 3728-32
Zotz RB, Giers G, Maruhn-Debowski B and Scharf RE. Genetic typing of human platelet antigen 1 (HPA-1) by oligoligation assay in a specific and reliable semi-automated system. Br J Haematol. 1997, 96 (1): 198-203
Eggerding FA, Iovannisci DM, Brinson E, Grossman P and Winn-Deen ES. Fluorescence-based oligonucleotide ligation assay for cystic fibrosis trnsmembrane conductance regulator gene mutations. Hum Mutation. 1995, 5 (2):153-65
Grossman PD, Bloch W, Brinson E, Chang CC, Eggerding FA, Fung S, Iovannisci DA, Woo S and Win-Deen ES. High-density multiplex detection of nucleic acid sequences: oligonucleotide ligation assay and sequence coded separation. Nuc Acid Res. 1994, 22 (21): 4527-34

Applied Biosystems web page :- http://www.appliedbiosystems.com/products/productdetail.cfm?id=118
Applied Biosystems Cystic Fibrosis Assay - Protocol

Schematic Diagram of the OLA/SCS Assay Technology

(From the ABI web page)

OLA diagram



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